New DMD Treatment Approved: Duvyzat

Greetings, here’s your MDA Newsletter [Muscular Dystrophy Association]( [MDA Monthly Newsletter] New Drug Approval for Duchenne Muscular Dystrophy [New DMD Drug Approval]( The Muscular Dystrophy Association’s funding of foundational research leads to [new drug approval by the US Food and Drug Administration (FDA)]( of Duvyzat (givinostat), a histone deacetylase (HDAC) inhibitor to treat children and adolescents living with Duchenne muscular dystrophy (DMD). This drug changes gene expression in cells by altering the three-dimensional folding of DNA and has shown that it can slow DMD progression. Duvyzat (givinostat) will be made available in the United States by ITF Therapeutics. [Read the Press Release]( --------------------------------------------------------------- Celebrating the Impact of Volunteers [Celebrating the Impact of Volunteers]( April is Volunteer Month, and at MDA, we’re celebrating the heart of our community: our volunteers. From advocacy to summer camps, fundraising events and program support, the contributions of MDA volunteers are essential in shaping the future for people living with neuromuscular diseases. Visit [mda.org/volunteer]( to learn more about the invaluable impact of our current volunteers and find opportunities to join us in this vital work. [Celebrate National Volunteer Month]( --------------------------------------------------------------- Volunteer Spotlight: Meet Marygrace! [Volunteer Spotlight: Marygrace]( Marygrace joined the MDA volunteer team after her grandson was diagnosed with a neuromuscular disease. Motivated by her personal connection and the desire to contribute to MDA’s efforts and support families like hers, Marygrace volunteered at the 2022 Twin Cities Muscle Walk. [Read More]( --------------------------------------------------------------- Get Ready to Vote in the 2024 Election [Get Ready to Vote in 2024]( The election might be months away, but it's never too early to prepare and ensure you can access the vote. Join MDA's Advocacy team on April 30 at 7pm ET and learn about the power of your vote in 2024. [Join Us]( Neuromuscular disease journeys don't need to be navigated alone — we're here to help! [VIsit the MDA Resource Center]( MDA Summer Camp is almost here! [MDA Summer Camp]( Only a few short months until we kick off another magical summer at MDA Summer Camp! Camper and volunteer applications for sessions taking place in June are due soon. Visit our website for the full list of camps. [Apply Today!]( --------------------------------------------------------------- Register for MDA’s Next Steps Seminar | April 23-24, 5-8 p.m. ET [Next Steps Seminar]( Have you or someone you know been diagnosed in the past two years with a neuromuscular disease? This free, virtual seminar provides pre-recorded and live presentations, interactive discussions, and a chance to connect with others to help navigate the decisions ahead. [Register Today!]( Read Quest Magazine. Listen to the Podcast. Follow the Blog. [Subscribe]( Join an MDA Community Group [Join an MDA Community Group]( As a member of the MDA Community, one of the many ways you can connect with others is by joining an MDA Community Group. Groups include Pediatric and Adult Newly Diagnosed groups, an ALS group for those living with ALS and their family members, and a Gene Therapy group for those eligible for current approved therapies. [Join Today!]( --------------------------------------------------------------- ICYMI - [NFL Running Back Nyheim Hines Supports Nation's Largest St. Patrick’s Day Fundraising Campaign to Benefit Muscular Dystrophy Association]( - [Corpus Christi Fire Department prepares for 'Fill the Boot' fundraiser]( - [Simply Stated: The Creatine Kinase Test]( - [MDA Ambassador Guest Blog: My Experience Participating in a Research Study]( - [NeuroVoices: Rita Sattler, MD, MSc, on 2024 MDA Conference and Advances in ALS Research]( - [Reaction to 2024 MDA Legacy Award: Jeff Chamberlain, PhD]( - [New Rules Would Protect Disabled Air Travelers]( - [Learn of the Important Advocacy Issues Fought on Behalf of People with Muscular Dystrophy]( --------------------------------------------------------------- Upcoming MDA Events For all upcoming public events, please visit [mda.org/events](. Next Steps Seminar: Newly Diagnosed - Adults Tuesday, April 23-24, 2024 | 5 - 8 p.m. ET [Register Here]( Support Us Monthly For just $19 a month, you can be a champion for kids and adults with neuromuscular diseases. Donate today to support research and programs for people living with neuromuscular disease. [Donate Monthly]( --------------------------------------------------------------- [Facebook]( [Twitter]( [Instagram]( [LinkedIn]( [YouTube]( [MDA.org]( © 2024 Muscular Dystrophy Association, Inc.. All rights reserved. 1016 W Jackson Blvd #1073 Chicago, IL 60607 1-800-572-1717 [Unsubscribe]( | [State Fundraising Notices]( The Muscular Dystrophy Association (MDA) is a qualified 501(c)(3) tax-exempt organization. [View Online]( | [Subscription Center]( | [Privacy Policy](